Lysogene Provides Additional Update on AAVance Phase 2/3 Gene Therapy Clinical Trial with LYS-SAF302 in children with MPS IIIA
Positive biomarker data confirmed in additional subjects and at additional timepoints Stable or continuously increasing cognitive, language and motor functions observed in patients treated at ≤31 months of age, including subjects with SGSH mutations associated with the severe disease phenotype Full data analysis in Q3 2022 before discussions with regulatory authorities on next steps PARIS–(BUSINESS … [Read more…]
