Azafaros Secures € 132M in Oversubscribed Series B Financing to Advance Phase 3 Clinical Programs of Innovative Therapies in Lysosomal Storage Disorders

Financing round led by Jeito Capital and co-led by Forbion Growth, with participation from Seroba, Pictet Group and other existing investors Proceeds to fund two Phase 3 pivotal programs with nizubaglustat, lead asset in Niemann-Pick disease Type C (NPC) and GM1/GM2 gangliosidoses as well as expanding the Azafaros pipeline to other indications Nizubaglustat has been … [Read more…]

Modalis has been selected as a finalist in the XPRIZE Healthspan FSHD Bonus Prize Competition and awarded research funds.

TOKYO & WALTHAM, Mass.–(BUSINESS WIRE)–Modalis Therapeutics Corporation (Tokyo Stock Exchange: 4883), a pioneering company developing innovative products for the treatment of rare genetic diseases utilizing its proprietary CRISPR-GNDM® epigenome editing technology, announced its recognition as a top eight finalist in the prestigious XPRIZE Healthspan competition’s FSHD Bonus Prize and award of $250,000 for demonstrating a … [Read more…]

Sangamo Therapeutics Reports Recent Business Highlights and First Quarter 2025 Financial Results

Announced capsid license agreement with Lilly to deliver genomic medicines for up to five central nervous system (CNS) disease targets. Received $18 million upfront license fee for first target and eligible to earn up to $1.4 billion in additional licensed target fees and milestone payments, plus tiered royalties on potential net sales. Announced derisking milestones … [Read more…]

Sangamo Therapeutics Postpones First Quarter 2025 Conference Call to Later the Same Day

RICHMOND, Calif.–(BUSINESS WIRE)–Sangamo Therapeutics, Inc. (Nasdaq: SGMO), a genomic medicine company, today announced that the first quarter earnings call originally scheduled for 4:30p.m. Eastern on Monday, May 12 will be postponed to 6:30p.m. Eastern on Monday, May 12, 2025. The registration and access link previously provided remains the same. Participants should register for, and access, … [Read more…]

Global Healthy Living Foundation Takes National 340B Reform and Transparency Briefing To New York

Chief Legal and Policy Officer, Steven Newmark, Joins Policy Briefing with Assemblymember Amanda Septimo and the Community Liver Alliance UPPER NYACK, N.Y.–(BUSINESS WIRE)–Steven Newmark, Chief Legal and Policy Officer of the Global Healthy Living Foundation (GHLF), takes the organization’s national 340B reform message to a policy briefing in Albany, NY, on May 13, addressing the … [Read more…]

Pharmaceutical Regulatory Affairs in China – 2 Day Online Training Course (June 25-26, 2025) | Unlock Pharmaceutical Success in China – ResearchAndMarkets.com

DUBLIN–(BUSINESS WIRE)–The “Pharmaceutical Regulatory Affairs in China Training Course (ONLINE EVENT: June 25-26, 2025)” has been added to ResearchAndMarkets.com’s offering. Explore the comprehensive landscape of pharmaceutical marketing authorization in China, including Hong Kong, Macau, and Taiwan, through this specialized two-day seminar. This seminar will provide an invaluable overview of how to gain and maintain a … [Read more…]

ImmunityBio Reports Doubled Net Revenue and 150% Unit Growth in Q1 2025, With Continued Strong Sales Momentum in First Quarter since J-code

For the three months ended March 31, 2025—marking the first quarter with a permanent J-code that streamlined billing and reimbursement for prescribing providers—ImmunityBio achieved net product revenue of approximately $16.5 million, representing a 129% increase over $7.2 million in Q4 2024. ANKTIVA® unit sales volume in Q1 2025 grew 150% over Q4 2024, with monthly … [Read more…]

Darling Ingredients and Tessenderlo Group Agree to Form New Company to Accelerate Growth in Attractive Collagen-Based Health, Wellness and Nutrition Sector

Creates ~$1.5 billion revenue company in fast-growing collagen-based health, nutrition and food sectors 85% owned and consolidated by Darling Ingredients Non-cash transaction, combining assets, capabilities Strengthens foundation around serving food and pharma customers Provides a platform for accelerated product development and growth Creates an opportunity to unlock significant shareholder value IRVING, Texas–(BUSINESS WIRE)–$DAR—Darling Ingredients Inc. … [Read more…]

InnoCare’s Mesutoclax Receives Breakthrough Therapy Designation from China’s NMPA

BEIJING–(BUSINESS WIRE)–InnoCare Pharma (HKEX: 09969; SSE: 688428), a leading biopharmaceutical company focusing on the treatment of cancer and autoimmune diseases, announced today that its B-cell lymphoma-2 (BCL2) inhibitor, Mesutoclax (ICP-248), has been granted Breakthrough Therapy Designation (BTD) by the Center for Drug Evaluation (CDE) of the China National Medical Products Administration (NMPA) for the treatment … [Read more…]

Nanyang Biologics and Precisya Global Inc Announce Strategic Collaboration to Validate Natural Compounds Against Genetic Disease Markers

SINGAPORE & WILMINGTON, Del.–(BUSINESS WIRE)–Nanyang Biologics (NYB) and Precisya Global Inc (PGI) announce a strategic collaboration to leverage our technologies in validating potential therapeutic benefits of natural compounds against genetically identified risk factors and predispositions for chronic diseases. The partnership combines PGI’s genomic big data analytics with NYB’s natural compound libraries and AI capabilities. The … [Read more…]